UPCOMING SESSIONS in ET
Tue, Sep 1, 2026
5:00 – 6:00 AM Bangkok
Understanding Your Care Journey: From Testing to Treatment Brian L. Miller II Click Here To Register
UPCOMING SESSIONS in ET
Tue, Sep 1, 2026 · 5:00 – 6:00 AM Bangkok
Understanding Your Care Journey: From Testing to Treatment
Brian L. Miller II
Click Here To Register
View all sessions

Clinical Trial Shows Promise of a Functional Cure for Sickle Cell Disease

Source
Technologynetworks Biopharma

Gene therapy eliminated pain and improved blood counts in most patients with sickle cell disease in a major trial.

New results from a clinical trial show promising outcomes for a gene-edited treatment for severe sickle cell disease, a genetic blood disorder with few curative options.