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Sickle cell disease—the subject of a new Seminar in The Lancet—is one of the most prevalent and fastest-growing genetic disorders worldwide. Although its true…

Advanced genomic technologies are revolutionizing our ability to understand complex diseases. Large‐scale population studies are needed to realize the potential of…

The purpose of this study is to evaluate the safety and tolerability, pharmacokinetics and pharmacodynamics, pH and food effect, and preliminary efficacy of BMS-…

The American Society of Gene and Cell Therapy is hosting this free virtual summit that will bring together patients, caregivers, advocates, researchers, and…

In the U.S., having sickle cell disease (SCD) continues to place a heavy clinical burden on patients, who often require multiple medications, frequent blood…

A woman whose blood donations are so rare they are frozen for up to 30 years said she feels "very special and honoured" to be able to help sick patients.Mina…

KEY MARKET INSIGHTSListen to Audio VersionThe global sickle cell disease treatment market size was estimated at USD 3.94 billion in 2025 and is projected to reach…

Of the estimated 515,000 infants born with sickle cell disease (SCD) each year around the world, many children in resource-limited settings experience early…

Sickle cell disease is often thought of solely as a blood disorder, but new research from the Wood Neuro Research Group provides measurable evidence that it can…

Myeloablative hematopoietic stem cell transplantation (HSCT) “resulted in stable pulmonary function” among pediatric patients with sickle cell disease (SCD),…