News

Agios Pharmaceuticals AGIO executives said the company is focused on advancing mitapivat across rare hematologic diseases, highlighting early launch traction in…

Despite rapid therapeutic advances in sickle cell disease, from red blood cell exchange to gene therapies, delivery remains constrained by infrastructure, geography…

AbstractIntroduction: Sickle cell disease is an inherited red blood cells disorder which leads to oxidative stress and resulting in the disturbance of energy…

State Minister for Women and Child Welfare and Tribal Welfare Gummidi Sandhyarani has said the government is committed to providing health security to every tribal…

Vishakhapatnam : In a first-of-its-kind initiative in the government hospital sector in Andhra Pradesh, the state government has established a 'Centre of Competence…

OverviewThe goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 injection in treating sickle cell disease. …

AbstractBackground: Sickle cell disease, a genetic blood disorder marked by vaso-occlusive crises and severe pain, presents a major global health challenge.…

Presented improved editing data in non-human primates (NHP) for sickle cell disease (SCD), demonstrating a single dose of Gene Writer achieved an average of 85% of…

Exclusive: Demand for blood to treat the rare disorder has soared by 132% in 10 yearsDemand for blood needed to treat rare disorders such as sickle cell has soared…

Agios Pharmaceuticals AGIO announced that it has submitted a supplemental new drug application (sNDA) to the FDA seeking accelerated approval for the label…