Clinical Trials and Research

AbstractIntroduction: Sickle cell disease (SCD) is a genetic condition with serious complications, frequently necessitating emergency medical attention. This study…

Fertility also improved, with 2 successful pregnancies after treatment: StudyNearly every person with sickle cell disease (SCD) who underwent a new regimen for stem…

AbstractIntroduction: Sickle cell disease is an inherited red blood cells disorder which leads to oxidative stress and resulting in the disturbance of energy…

AbstractBackgroundSickle cell disease (SCD) constitutes a significant public health concern in the Kingdom of Saudi Arabia (KSA), affecting a substantial proportion…

Sickle cell disease (SCD) is a prevalent hereditary hemoglobinopathy characterized by hemoglobin S (HbS) polymerization, resulting in chronic hemolysis, vaso-…

Sickle cell disease (SCD) is associated with severe systemic complications and increased mortality risk. Predicting SCD severity is currently difficult because of a…

OverviewThe goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 injection in treating sickle cell disease. …

AbstractBackground: Sickle cell disease, a genetic blood disorder marked by vaso-occlusive crises and severe pain, presents a major global health challenge.…

Presented improved editing data in non-human primates (NHP) for sickle cell disease (SCD), demonstrating a single dose of Gene Writer achieved an average of 85% of…

AbstractSickle cell-beta thalassemia, a compound heterozygous hemoglobinopathy, can be difficult to diagnose because clinical features and laboratory findings often…